E&C Markup- Chairwoman Rodger-Pediatric Priority Review Voucher

At the Energy and Commerce Health Subcommittee’s markup of 23 pieces of legislation, Members highlighted the need to reauthorize the Rare Pediatric Priority Review Voucher (PPRV) ahead of its September 30th expiration. Chairwoman McMorris Rodgers (R-WA) shared the story of the Dion family, who has been in D.C. this week advocating for the PPRV. Peter and Maggie Dion were diagnosed with a rare form of muscular dystrophy, Limb-Girdle Muscular Dystrophy, when they were 9 and 6, respectively. Without the Rare Pediatric Disease Priority Review Voucher Program, Maggie and Peter’s parents say their chances of getting treatments for their kids becomes almost impossible as there are over 30 subtypes of the disease – each requiring a different gene therapy. BIO supports the Creating Hope Reauthorization Act (H.R. 7384) which would reauthorize the PPRV and was pleased to see legislation to reauthorize the PPRV for 6 years pass the health subcommittee by a bipartisan vote. As members on both sides of the aisle shared, the PPRV is a critical tool in incentivizing the development of treatments for rare pediatric diseases. BIO urges Congress to sign this legislation into law before its expiration at the end of the fiscal year.
(May 16, 2024)

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